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Charcot-Marie-Tooth Disease (CMTD)
Types
Type 1 (60%) – CMT1 mutation (Demyelinating)
Type 2 (30%) – CMT2 mutation (Axonal)
Mixed (10%)
Presentation
The disease is length-dependent, therefore it usually presents during puberty. Clinical features include:
Slowly progressive distal symmetrical sensorimotor polyneuropathy
Symmetrical, distal muscular atrophy (champagne bottle legs, claw hand)
Pes cavus (club foot)
Reduced reflexes and tone
Investigations
NCS - Depends on the type of CMT mutation:
Demyelinating (T1) – ↓nerve conduction velocity
Axonal (T2) – ↓action potential amplitude
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